Enzyme Replacement Therapy

Monitoring the clinical and biochemical response to enzyme replacement therapy in three children with Fabry disease

监测3例法布莱病患儿对酶替代疗法的临床及生化反应

Sufficient and high activity GLA is the fundamental prerequisite for enzyme replacement therapy .

而获得足量、高活性的GLA是进行酶替代疗法的关键。

A retrospective study on enzyme replacement therapy in patients with Gaucher disease

酶替代治疗戈谢病72例

Effectiveness of enzyme replacement therapy to patients with Gaucher Disease

酶制剂Cerezyme治疗高雪氏病效果观察

Cardiac Findings After Enzyme Replacement Therapy for Mucopolysaccharidosis Type I

黏多糖贮积症I型酶替代治疗后的心脏改变

Enzyme replacement therapy in severe fabry with renal failure : A 1-year follow - up

酶替代疗法治疗1例严重Fabry肾衰竭的1年随访研究

Most CF patients have severe exocrine pancreatic insufficiency and must take pancreatic enzyme replacement therapy , the authors note .

作者注意到，大部分CF患者伴有严重胰腺外分泌功能不全，而且必须采取胰酶替代治疗。

Pharmacokinetic profile of recombinant human N-acetylgalactosamine 4-sulphatase enzyme replacement therapy in patients with mucopolysaccharidosis VI ( Maroteaux-Lamy syndrome ): A phase I / II study

人类N-乙酰半乳糖胺4-硫酸酯酶重组体在黏多糖病Ⅵ型（马-拉二综合征）患者替代疗法中的药物代谢动力学模式：一项Ⅰ/Ⅱ期研究

With the development of hematopoietic stem cell transplantation and enzyme replacement therapy , MPS have become treatable genetic metabolic diseases . In order to improve prognosis , it is crucial to diagnose and treat MPS in early phrases .

随着造血干细胞移植及酶替代治疗的逐步开展，MPS成为可治疗的遗传代谢病，早期诊断和早期治疗是改善预后的关键。